Latest posts tagged with #HCRU on Bluesky
Generating #RWE in #SpinalMuscularAtrophy (#SMA) faces hurdles with evolving standard of care, inconsistent outcomes measurement, severity baseline, and the need for long-term follow-up. Test your objectives with us: buff.ly/Qj6Z6Uq
#HCRU #SpinalCare #RealWorldEvidence
Generating #RWE in #SpinalMuscularAtrophy (#SMA) faces hurdles with evolving standard of care, inconsistent outcomes measurement, severity baseline, and the need for long-term follow-up. Test your objectives with us: buff.ly/Qj6Z6Uq
#HCRU #SpinalCare #RealWorldEvidence
Multifocal motor neuropathy (MMN) is often misdiagnosed as other conditions. How does that affect outcomes in patients who ultimately receive an MMN diagnosis?
Multifocal motor neuropathy (MMN) is often misdiagnosed as other conditions. How does that affect outcomes in patients who ultimately receive an MMN diagnosis?
jheor.org/article/140817
#HEOR #raredisease #HCRU
New in JHEOR: The third in a series of articles on glycogen storage disease type Ia explores the burden of this disease, including UK's NHS resource use and patient mortality. #HEOR #rarediseases #NHS #HCRU
New in JHEOR: The first in a series of three articles taking a deep dive into the costs, burden of disease, and quality-of-life issues associated with glycogen storage disease type Ia, a rare inherited disease. #jheor #rarediseases #GSDIa #HCRU #geneticdiseases
jheor.org/article/125886
