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#CPS1
Latest posts tagged with #CPS1 on Bluesky
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Posts tagged #CPS1
Baby KJ, the first person ever to undergo personalized #GeneEditing, took his first steps! ❤️
Babies with #CPS1 have a 50% chance of living past one week. This week, thanks to years of #RareDisease research, investment and advocacy, KJ will celebrate his second Christmas. people.com/first-baby-t...
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New Piece is LIVE!
Retro Revival is back for #Halloween, discussing Ghouls 'n Ghosts for #CPS1 through #Capcom Arcade Stadium and the #MegaDrive/#Genesis via the NSO classics for #NintendoSwitch
Check it out to learn more about this classic arcade game
wkohakumedia.com/2025/10/17/r...
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Three Wonders -- Midnight Wanderers (1991) (Run And Gun) (Arcade) [FULL LONGPLAY] [EN] [HD]
#retrogaming #MidnightWanderers #Arcade #CPS1 #ThreeWonders #runandgun #1991 #jgo #johnnygameover #videogame #longplay #gameplay #games #gaming #Capcom
www.youtube.com/watch?v=NTFx...
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![Megaman Power Battle [CPS1] - Crashman (Locrian)](https://cdn.bsky.app/img/feed_thumbnail/plain/did:plc:jgimt65pqgbljtjp3tiypgfk/bafkreig6mujkacocry2x6gdj6efp5psvln3itf5kfv7nj4tbn2byuozya4)
Megaman Power Battle [CPS1] - Crashman (Locrian)
#megaman #rockman #megamanthepowerbattle #crashman #cps1 #arcade #vgm #bgm #ost #soundtrack #gaming #gamemusic #videogamemusic #locrian #locrianscale #locrianvgm #locrianmusic #locrianmode #ロックマン #ロックマン・ザ・パワーバトル #ロクリアン
youtube.com/watch?v=MwIv...
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Here's this week's #retrorgbweeklyroundup! Search any video or podcast app for RetroRGB Weekly, or head to the main link: www.retrorgb.com/week477.html
.
#retrorgb #classicgaming #retrogaming #retroworldexpo #MiSTerFPGA #PhilipsHue #VirtuaFighter #cps1 #ShinreiJusatsushi #GBAeReader
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![Three Wonders -- Midnight Wanderers (1991) (Run And Gun) (Arcade) [FULL LONGPLAY] [EN] [HD]](https://cdn.bsky.app/img/feed_thumbnail/plain/did:plc:gxobxxqwqcrku57msewznmag/bafkreibp7vflddks53bkyhvas55o3cworkvpyhkazftgipusf7zthnfz7a)
Three Wonders -- Midnight Wanderers (1991) (Run And Gun) (Arcade) [FULL LONGPLAY] [EN] [HD]
#retrogaming #MidnightWanderers #Arcade #CPS1 #ThreeWonders #runandgun #1991 #jgo #johnnygameover #videogame #longplay #gameplay #games #gaming #Capcom
www.youtube.com/watch?v=NTFx...
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![[INSERT COIN] Magic Sword (1990) (Hack And Slash) (ARCADE) [EN] [HD]](https://cdn.bsky.app/img/feed_thumbnail/plain/did:plc:gxobxxqwqcrku57msewznmag/bafkreihpaofdykyd6z4bx7euxmlhm6b4akrgv2pfysjudhju2mo54tu6am)
[INSERT COIN] Magic Sword (1990) (Hack And Slash) (ARCADE) [EN] [HD]
#retrogaming #MagicSword #Arcade #CPS1 #action #hackandslash #1990 #jgo #johnnygameover #videogame #demo #intro #gameplay #games #gaming #HowToPlay #InsertCoin #Capcom
www.youtube.com/watch?v=cNJX...
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![Mega Drive Longplay [439] The Great Circus Mystery starring Mickey and Minnie](https://cdn.bsky.app/img/feed_thumbnail/plain/did:plc:5rty3hrsetkhncq23a7qr777/bafkreidaaczc5vjzh6dzs3q6u4cuygemskewqngd3xuzywkga4hx2kw4nm)
I won’t deny that the SNES version of The Great Circus Mystery is superior, however being that this is a #CAPCOM game, I’ve taken a liking more towards the Genesis version because the music in it sounds like what you’d hear in a #CPS1 title. youtu.be/HjAjvt6d3qw
#MickeyMouse #Disney
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Mit einem neuen gentechnischen Verfahren korrigierten Forschende einen #Gendefekt, der zu einer schweren Störung im #Harnstoffzyklus und zu #Hirnschäden führt. Nach der Therapie konnte das behandelte Kind die Dosis Stickstoff-bindender Arzneien reduzieren und mehr Protein konsumieren. #medsky #CPS1
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We are pleased to announce that we are launching a two-year project to establish the NUCDF Partner Network and develop a roadmap for future research in urea cycle disorders #UCDs #PatientEngagement #OTC #CPS1 #ASA #ASS1
nucdf.org/partner-netw...
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Gene editing used in vivo to treat CPS1 deficiency in a child.
Editorial by Rahman & Baruteau reflects on what this means for IMDs.
🔗 doi.org/10.1002/jimd...
#IMD #GeneEditing #CPS1 #JIMD
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Discover how Ayurveda’s Garbh Sanskar supports a healthy pregnancy and may reduce genetic risks like CPS1 deficiency. Ancient wisdom for modern prenatal care! 🌿
Read more:
ayurvedasandeep.wordpress.com/2025/05/29/a...
#Ayurveda #GarbhSanskar #HealthyPregnancy #CPS1 #HolisticHealth
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#MedNews - A customized gene-editing approach has been used for the first time to treat severe #CPS1 deficiency, a rare genetic condition, in an infant.
Full story 👉 buff.ly/930Deib
#GeneEditing #GeneTherapy #PediatricMed #MedSky
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Personalized gene editing corrects fatal infant metabolic disorder in world-first treatment www.news-medical.net/news/2025052... #geneediting #CPS1 #genetics #metabolism #CRISPR #precisionmedicine #biotechnology #medicine @nejm.org
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In soli sei mesi, un team di ricercatori ha sviluppato e somministrato una terapia a base di #editingGenomico progettata su misura per un bambino affetto da una rara malattia metabolica
#crispr #cps1
www.osservatorioterapieavanzate.it/terapie-avan...
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Baby KJ with #CPS1 deficiency was successfully treated using custom #GeneEditing therapy at @childrensphila.bsky.social, a NORD Center of Excellence. Dr. Kiran Musunuru, developer of the #CRISPR #GeneTherapy, will speak at NORD’s Rare Disease Symposium! nordscience.org
Read the story: n.pr/3YTUmUx
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Prima terapia al mondo con l'editing genetico su misura. Su un bambino di pochi mesi con una rara malattia metabolica. #CPS1 #Crispr #editinggenetico #iperammoniemia #malattiegenetiche
scienzamagia.eu/sociale-coll...
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WHAT...A...WEEK!
Landmark ATTR-Polyneuropathy Data by Intellia Caps Off Momentous Week in #CRISPR Therapeutics (blog): rnaitherapeutics.blogspot.com/2025/05/land...
#CPS1 #Musunuru $NTLA $PRME $VERV $BEAM $PRQR
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#CPS1 shorts getting nervous. #PrimeMedicine after-hours showed it.
#FDA cutting red tape (see also dropping certain preclinical animal study requirements) is continuing+could dramatically shorten timelines+costs making sector investable again. #CRISPR + #oligos predestined. Monday!
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Now $2 after-hours. Squeeze or still digesting #CPS1? #PrimeMedicine
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#PrimeMedicine, arguably main beneficiary of #CPS1 CRISPR story yesterday up +10%+ today. Just saying.
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A figure from the paper Patient-Specific In Vivo Gene Editing to Treat a Rare Genetic Disease
What an incredible day with work from the Children Hospital of Philadelphia, @pennmedicine.bsky.social and their colleagues!
First-ever personalized #LNP -based #CRISPR #GeneTherapy for the rare genetic condition carbamoyl-phosphate synthetase 1 ( #CPS1) deficiency.
www.nejm.org/doi/full/10....
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The #CPS1 deficiency #CRISPR story will be one of the prouder accomplishments also by #FDA rank and file.
I doubt that just because #PeterMarks had been involved, new leadership will kill the approach and make patient access harder. Could be transformational for genetic drug developers.
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Assembled the #darksoft #cps1 #multikit. Strong recommend: get a prom chip puller, makes your life easier. I hate using a flathead to remove prom.
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Quiz Time!
Parmi ces 3 machines, CPS1, Megadrive ou SNES, une seule est capable d’afficher un sprite de la taille de l’écran, laquelle?
Réponse en dessous ^^ 👇
#Quiz #Megadrive #SNES #CPS1
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King of Dragons, Dragon Blaze, Ninja Spirit, and Shock Troopers on #TheAfterHoursArcade! #cps1 multi, #psikyo multi, #irem M72 Multi, and the #MiSTerFPGA! https://www.twitch.tv/gillaxian 9pm PST start
#retrogaming #twitchstreamer #arcade #candycab #chillstream #neogeo #smallstreamer
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